Drug That May Treat Incurable Neurodegenerative Disease Moves Forward
With its potentially breakthrough drug, Ionis Pharmaceuticals is targeting Huntington’s disease, which causes uncontrollable movements and problems with emotions and cognition, along with changes in personality.
San Diego Union-Tribune:
Potential Breakthrough Drug For Huntington's To Enter Advanced Clinical Testing
A potential breakthrough drug for treating Huntington’s disease from Carlsbad’s Ionis Pharmaceuticals will begin an advanced clinical trial early next year. If successful, the trial could lead to marketing approval. Ionis partner Roche, which is handling the clinical trials, made the announcement Sunday. The trial will take place globally. Huntington’s disease is an incurable and invariably fatal neurodegenerative disease caused by mutations in one gene. More than 30,000 Americans have the mutation, and either have the disease or will eventually develop it. (Fikes, 9/17)